The Evolving Landscape of Novel Therapies for Hemophilia: What’s Here & What’s Coming?

On this episode we talk with experts Dr. Amy Shapiro, Dr. Maria Elisa Mancuso, Dr. Steve Pipe, Dr. Johnny Mahlangu, and Dr. Lynn Malec to delve into the ongoing evolution of hemophilia therapies. The discussion highlights recent advancements in treatments such as emicizumab, extended half-life factor VIII therapies, and investigates medications in clinical trials like Concizumab, Marstacimab, and Fitusiran. The episode also reflects on the role of treatment individualization and the need for more inclusive research data.

Contributors:

Johnny Mahlangu, MBBCh, MMed, FCPath

Lynn Malec, MD, MSc

Elisa Mancuso, MD

Steven Pipe, MD

Amy Shapiro, MD

Senior Advisor: Donna DiMichele, MD

Hosted & Written by: Patrick James Lynch

Featured Advertiser:

Sanofi

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Show Notes: